In May 2025, the Advisory Committee on Heritable Disorders in Newborns and Children (ACHDNC) plans to vote on whether to Approved Therapies & Sequential Therapy – PPMD 2025 Annual Conference · You may also like · Research · Advocacy · Care · Community
Opening Session: Welcome to PPMD's 2025 Annual Conference Pat Furlong, Founding President & CEO, PPMD. PPMD 2025 Annual Conference: Day 2 - Dystrophin: The Missing Muscle Protein
2025 PPMD Annual Conference Archives - Parent Project Muscular The PPMD Conference is over, and this is an honest conversation where we unpack our biggest takeaways from the 3-day PPMD
Deramiocel (CAP-1002) for FDA Approval Taking Charge of Your Future: A PAAC Presentation Pat Moeschen, Advisor, PPMD Adult Advisory Committee.
Parent Project Muscular Dystrophy ("PPMD") hosts conferences, meetings, and webinars which bring together clinicians, researchers, industry leaders, government PPMD 2025 CONFERENCE AGENDA. Wednesday, June 18. 3:00p-5:30p. Newly Diagnosed Family Meeting. (private session). Breakout Room 1. 3:00p-5:30p. Childcare for
A little over a month ago I went to the annual Parent Project Muscular Dystrophy (PPMD) Conference. This video is a look into my What Experts Are Saying About Stem Cell Research for Duchenne | PPMD Conference Panel
Duchenne PPMD Conference Dance Party Vibes 💚🕺💃💚 #dmd #duchenne #medicalconference #party PPMD 2025 Annual Conference: Day 2 - Navigating Behaviors: Strategies for Support & Success
Going to the 2025 PPMD Conference! Gene Therapy Overview with Dr. Kevin Flanigan
Jeff Galvin Presents "Discovering The Clinical & Commercial Potential of Cell and Gene Therapy" at the Databridge (DBMR) We're back from the PPMD conference in Vegas and right back to real life. Today's PT session with Jack… well, let's just say he's
A New Take on the Ins and Outs Moderator: Kent Williams, MD • Swallowing Throughout the Lifespan Kiera Berggren, CCC-SLP, PPMD 2025 Annual Conference: Day 3 - How MRI is Advancing Drug Development for Duchenne
PPMD 2025 Annual Conference: Day 2 - How do We Get to the Next Step in Research? The DCRN Explained Nurturing Mental Wellness in Everyday Life Kristy Lewandowski, MA, CCC-SLP.
Keynote Address: Meeting the Challenge of Rare Disease: 25 Years of Lessons Learned Albert Freedman, PhD. Bob Butchofsky, CEO speaks for Mati Therapeutics during the Innovative Showcase at OIS@ASCRS 2019. REGISTER for our What Experts Are Saying About Stem Cells & Duchenne | PPMD conference. #stemcells #dmd #genetherapy
PPMD Annual Conference - Parent Project Muscular Dystrophy Sarepta Therapeutics recently joined PPMD for a community webinar to share details from the company's recent safety update on New Treatment for Duchenne Muscular Dystrophy Patients | Cedars-Sinai
On November 14, 2016, PPMD hosted a webinar with Masters Pharmaceuticals. The discussion was around the transition from 2025 PPMD Duchenne Conference in Vegas | Family Vlog + Weekend Recap Liz Parrish, the Founder and CEO of BioViva Sciences USA Inc, is best known for recently becoming the first person to be treated
The PPMD Adult Advisory Committee (PAAC) was joined by Mike Verrette on March 31, 2021 for a conversation about gaming PPMD 2025 Annual Conference: Day 1 - A New Era of Steroids, Endocrinology & Emergency Care Breakfast Banter: Building Friendships and Self Advocacy Skills (Panel Discussion) Moderator: Patrick Moeschen Panelists: Jill
PPMD 2025 Annual Conference: Day 3 - Finding Light in the Journey Handmade Conference
Panel Discussion: Fertility & Family Planning At the PPMD Family Conference, we listened to an expert panel discuss stem cell research and what it could mean for Duchenne
5 ways to Advocate for Your child's IEP !! Dads Virtual Meeting | December 2025 2026 Disney Princess Half Marathon Weekend. February 26 - March 2, 2026. > PPMD's 25th Annual Advocacy Conference.
PPMD 2025 Annual Conference: Day 1 - A New Era in Duchenne & Becker Muscular Dystrophy Reggie Fils-Aime wins E3 in Less than One Minute
Michael Byrne, PhD, Director in Vivo Biology, Ophthalmology speaks on Wave Life Sciences' Exciting Research Project Funded © 2025 Parent Project Muscular Dystrophy | Contact Us | Privacy Policy | EIN 31-1405490. 1-800-714-5437 | info@parentprojectmd.org | 1012 14th Street, NW Our Biggest Takeaways from PPMD 2024
The Impact of Diagnosis: Managing Family Dynamics - Panel Discussion Moderator: Pat Furlong Panelists: Heather Hay, Tristan PPMD 2025 Annual Conference: Day 3 - Therapies that Slow Progression
PPMD 2025 Annual Conference: Day 2 - Exercise: How Much is Too Much? Why We're Taking a Break from Physical Therapy | Duchenne Life
Aging (Aging-US) published this trending research paper on July 16, 2020, entitled, "Activation of C-reactive protein A cell therapy developed by the executive director of the Smidt Heart Institute stabilizes weakened muscles–including the heart
Pancreatic Cancer Webinar Recording pssst hey, it happened: Smash Bros. Melee's Juan "Hungrybox" Debiedma's PPMD 2025 Annual Conference: Day 2 - Meeting the Challenge of Rare Disease: 25 Years of Lessons
The board is meeting via teleconference and anyone wishing to listen to the meeting may dial in to the conference call-in number. Approved Drugs and Sequential Therapy: Discussing Catalyst Pharmaceuticals, ITF Therapeutics, NS Pharma, PTC Therapeutics, PPMD 2025 Annual Conference: Day 2 - Building Friendships & Self Advocacy Skills
Sarepta Therapeutics: Safety Update on ELEVIDYS in Non-Ambulatory Individuals Living with Duchenne PPMD 2025 Annual Conference: Day 3 - A New Take on the Ins and Outs Neuromuscular specialist Professor Jenny Morgan presents on the new advances in stem cell research for muscular dystrophy,
PPMD's Duchenne Early Intervention Symposium | March 2025 Our 2025 Advocacy Conference will be held at The Dupont Hotel in Washington, DC, March 9-11. The schedule will include: Sunday, March 9th
PPMD & PEAL's 2025 Wrightslaw Special Education Law Event Archive - Parent Project Muscular Dystrophy Cell and Gene Therapy: Discovering The Clinical & Commercial Potential - Jeff Galvin Webinar
Updates in Research and Care for Carriers Moderator: Mena Scavina, DO • Carrier Provider Screening and Practices: Survey Cell and Gene therapies are an emerging form of healthcare that offer significant potential to improve the practice of medicine and
PPMD 2025 Annual Conference: Day 1 - Exploring the Gene Therapy Landscape Connect With #ExpressoShow Online: Website: FACEBOOK: Finding Light in the Journey: Fostering Resilience, Gratitude & Hope Rebecca J Scharf, MD, MPH, University of Virginia Medical
RESOURCE - As dedicated parents of an autistic child, I am determined to raise awareness and shed light Exercise: How Much is Too Much? Moderator: Sue Apkon, MD. What to Know About Exercise in Duchenne- Tanja Taivassalo, PhD. Working With Your PT PPMD 2025 CONFERENCE AGENDA
PPMD Advocacy Conference 2025 - Campaign Mati Therapeutics - Innovation Showcase at Ophthalmology Innovation Summit @ ASCRS 2019 Shadow Boxing
Stem Cell therapy - pioneering treatment for muscular dystrophy Navigating Behaviors: Strategies for Support and Success Moderator: Colleen Labbadia • Duchenne and The Brain Natalie Truba Approved Therapies & Sequential Therapy - PPMD 2025 Annual
PPMD 2025 Annual Conference: Day 1 - Empowering Families through Community, Care & Research PPMD #1 – Special Meeting Agenda, December 8, 2025 - Forest
PPMD 2025 Annual Conference: Day 3 - Taking Charge of Your Future: A PAAC Presentation Wave Life Sciences on Exciting Research Projects Funded by the Foundation Fighting Blindness This event has passed. PPMD & PEAL's 2025 Wrightslaw Special Education Law & Advocacy Conference. September 18 @ 9:00 am - 4:
PPMD 2025 Annual Conference: Day 2 - Nurturing Mental Wellness in Everyday Life PPMD is excited to host the sixth in-person Duchenne Healthcare Professionals Summit in San Diego, California, January 15-17.
Exploring the Landscape of Gene Therapy Moderator: Eric Camino, PhD Gene Therapy Overview: How We Got Here and Where PPMD 2025 Annual Conference: Day 1 - The Impact of Diagnosis: Managing Family Dynamics
PAAC Chats: Gaming and Disability PPMD Hosts 2025 Duchenne Healthcare Professionals Summit in
TEDxUniversityofPretoria Annual Conference Theme Reveal 2020 PPMD 2025 Annual Conference: Day 3 - Updates in Research & Care for Carriers A New Era of Steroids and Endocrinology Care Moderator: Rachel Schrader, MS, APRN, CPNP-PC The Evolving Steroid
This June, we took our son Mason to Las Vegas for our THIRD PPMD conference! It was a weekend full of emotions, connection, Therapies that Slow Progression Moderator: Eric Camino, PhD • Understanding Cell Therapies: What They Are, What They Aren't
Duchenne 101 Discussions Stronger Together: Empowering Families Through Community, Care, and Research Moderator: Molly Dystrophin: The Missing Muscle Protein Moderator: Eric Camino, PhD • Understanding Dystrophin Expression Stan Nelson, MD
How Do We Get To The Next Step in Research: The DCRN Explained Megan Freed, MPH, PPMD. Difference between Deloitte India and Deloitte USI
PPMD 2025 Annual Conference: Day 1 - Trials & Treatments: Making Decisions that are Right for You Making Decisions That Are Right For You (Panel Discussion) Moderator: Sue Apkon, MD Panelists: Maru Chapur, Winston Choi, Advanced therapeutics 2025: Translation and commercialisation of cell & gene therapy products
Aging-US | Age-related Macular Degeneration and C-reactive Protein Gene therapy to save the world Exercise: How Much is Too Much? - 2025 PPMD Annual Conference
Cardiac Management Throughout the Lifespan Moderator: Linda Cripe, MD • Creating New Standards Carol Wittlieb-Weber, MD Exercise: How Much is Too Much? Moderator: Sue Apkon, MD • What to Know About Exercise in Duchenne Tanja Taivassalo, PPMD 2025 Annual Conference: Day 2 - Approved Therapies & Sequential Therapy
Register for 2018: Learn to make soap PPMD 2025 Annual Conference: Day 3 - Cardiac Management Throughout the Lifespan [Webinar] Deflazacort Access: Navigating Potential Changes to Your Prescription - November 2016
Unaffiliated, unsponsored, unpaid. For the love of the patients and families dealing with DMD. Time is muscle. Let's get this How MRI is Advancing Drug Development for Duchenne Krista Vandenborne, PhD, University of Florida.